Glycogen reduction in myotubes of late-onset Pompe disease patients using antisense technology
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Glycogen reduction in myotubes of late-onset Pompe disease patients using antisense technology
Goina E, Peruzzo P, Bembi B, Dardis A, Buratti E. Glycogen reduction in myotubes of late-onset Pompe disease patients using antisense technology. Mol Ther. 2017;[Epub ahead of print] doi:10.1016/j.ymthe.2017.05.019
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