A single administration of morpholino antisense oligomer rescues spinal muscular atrophy in the mouse
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A single administration of morpholino antisense oligomer rescues spinal muscular atrophy in the mouse
Porensky PM, Mitrpant C, McGovern VL, Bevan AK, Foust KD, Kaspar BK, Wilton SD, Burghes AHM. A single administration of morpholino antisense oligomer rescues spinal muscular atrophy in the mouse. Hum. Mol. Genet. 2011;[Epub ahead of print] doi:10.1093/hmg/ddr600
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