Gene therapy rescues cilia defects and restores olfactory function in a mammalian ciliopathy model
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Gene therapy rescues cilia defects and restores olfactory function in a mammalian ciliopathy model
McIntyre JC, Davis E, Joiner A, Williams CL, Tsai IC, Jenkins PM, McEwen DP, Zhang L, Escobado J, Thomas S, Szymanska K, Johnson CA, Beales PL, Green ED, Mullikin JC, NISC Comparative Sequencing Program, Sabo A, Muzny DM, Gibbs RA, Attie-Bitach T, Yoder BK, Reed RR, Katsanis N, Martens J. Gene therapy rescues cilia defects and restores olfactory function in a mammalian ciliopathy model. Nat Med. 2012;[Epub ahead of print] doi:/10.1038/nm.2860
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