Targeted Exon Skipping to Correct Exon Duplications in the Dystrophin Gene
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Targeted Exon Skipping to Correct Exon Duplications in the Dystrophin Gene
Greer KL, Lochmüller H, Flanigan K, Fletcher S, Wilton SD. Targeted Exon Skipping to Correct Exon Duplications in the Dystrophin Gene. Molec Ther Nucleic Acids. 2014;3,e155. doi:10.1038/mtna.2014.8
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