Antisense Oligonucleotide-Based Therapy in Human Erythropoietic Protoporphyria
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Antisense Oligonucleotide-Based Therapy in Human Erythropoietic Protoporphyria
Oustric V, Manceau H, Ducamp S, Soaid R, Karim Z, Schmitt C, Mirmiran A, Peoc'h K, Grandchamp B, Beaumont C, Lyoumi S, Moreau-Gaudry F, Guyonnet-Dupérat V, de Verneuil H, Marie J, Puy H, Deybach JC, Gouya L. Antisense Oligonucleotide-Based Therapy in Human Erythropoietic Protoporphyria. Am J Hum Genet. 2014 Mar 26. pii: S0002-9297(14)00068-8. doi: 10.1016/j.ajhg.2014.02.010. [Epub ahead of print]
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