Systemic peptide-mediated oligonucleotide therapy improves long-term survival in spinal muscular atrophy
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Systemic peptide-mediated oligonucleotide therapy improves long-term survival in spinal muscular atrophy
Jon Moulton Mon Sep 19, 2016 4:34 pm
Hammond SM, Hazell G, Shabanpoor F, Saleh AF, Bowerman M, Sleigh JN, Meijboom KE, Zhou H, Muntoni F, Talbot K, Gait MJ, Wood MJ. Systemic peptide-mediated oligonucleotide therapy improves long-term survival in spinal muscular atrophy. Proc Natl Acad Sci U S A. 2016 Sep 12. pii: 201605731. [Epub ahead of print]
Jon Moulton- Posts : 5721
Join date : 2010-03-12
Age : 61
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